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2017 Standards of Care for Spinal Muscular Atrophy (SMA) | Internal Links | Dofollow |
The Guide to the 2017 International Standards of Care for SMA | Internal Links | Dofollow |
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Standards of Care for Congenital Myopathy (CM) | Internal Links | Dofollow |
Family guide for congenital myopathy | Internal Links | Dofollow |
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Family guide in different languages | Internal Links | Dofollow |
Standards of care for DM1 | Internal Links | Dofollow |
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EMA DMD workshop | Internal Links | Dofollow |
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MyoGrad graduate program in myology | Internal Links | Dofollow |
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Congenital Muscle Disease International Registry | Internal Links | Dofollow |
Global Registry for COL6-related dystrophies | Internal Links | Dofollow |
Congenital myasthenic syndromes | Internal Links | Dofollow |
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GNE Myopathy patient registries | Internal Links | Dofollow |
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MTM and CNM Registries | Internal Links | Dofollow |
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TREAT-NMD Core Datasets | Internal Links | Dofollow |
Core Dataset for Spinal Muscular Atrophy (SMA) | Internal Links | Dofollow |
DMD Expanded Core Dataset | Internal Links | Dofollow |
Core Dataset for Duchenne Muscular Dystrophy (DMD) | Internal Links | Dofollow |
Core Dataset for Facioscapulohumeral Muscular Dystrophy (FSHD) | Internal Links | Dofollow |
Core Dataset for Myotonic Dystrophy (DM) | Internal Links | Dofollow |
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Early Access to Medicines in Development | Internal Links | Dofollow |
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Myotubular and Centronuclear Myopathies | Internal Links | Dofollow |
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TREAT-NMD Newsletter – December 2020 | Internal Links | Dofollow |
TGDOC Quarterly Newsletter – Autumn 2020 | Internal Links | Dofollow |
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online form | Internal Links | Dofollow |
online form. | Internal Links | Dofollow |
Hebrew DMD Family Care Guide 2018 | Internal Links | Dofollow |
Mapping the differences in care for 5,000 Spinal Muscular Atrophy patients, a survey of 24 national registries in North America, Australasia and Europe | Internal Links | Dofollow |
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Common protocols in MDC1A preclinical research | Internal Links | Dofollow |
The Diagnosis & Management of DMD in different languages | Internal Links | Dofollow |
Creation of the DMD care standards document | Internal Links | Dofollow |
Guide for Families in different languages | Internal Links | Dofollow |
DMD standards of care now available on tablets and smartphones | Internal Links | Dofollow |
Family guide on Android App | Internal Links | Dofollow |
European neuromuscular fellowship core curriculum | Internal Links | Dofollow |
European Neuromuscular Core Curriculum update July 2011 | Internal Links | Dofollow |
Japanese GNE Myopathy Registry | Internal Links | Dofollow |
The Dysferlin Registry | Internal Links | Dofollow |
Global FKRP Registry | Internal Links | Dofollow |
Family Registry for Centronuclear and Myotubular Myopathies | Internal Links | Dofollow |
Hope versus hype: an online guide | Internal Links | Dofollow |
Cord blood banking | Internal Links | Dofollow |
SOP’s for cell lines | External Links | Dofollow |
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World Duchenne Organisation’s weekly online webinars | External Links | Dofollow |
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